Ultragenyx Pharmaceutical Inc.
Novato, USA
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Ultragenyx is a biopharmaceutical company committed to bringing novel therapies to patients for the treatment of serious rare and ultrarare genetic diseases. The company has built a diverse portfolio of approved medicines and treatment candidates aimed at addressing diseases with high unmet medical need and clear biology, for which there are typically no approved therapies treating the underlying disease. The company's product DTX401 is an investigational AAV8 gene therapy designed to deliver...